Tag Archives: disease

FDA Approves Oxbryta (voxelotor) for the Treatment of Sickle Cell Disease

FDA Approves Oxbryta (voxelotor) for the Treatment of Sickle Cell Disease Print this page November 25, 2019 — Today, the U.S. Food and Drug Administration granted accelerated approval to Oxbryta (voxelotor) for the treatment of sickle cell disease (SCD) in adults and pediatric patients 12 years of age and older. “Today’s approval provides additional hope… Read More »

Researchers discover potential new treatment for rare muscle-wasting disease

A team of Cardiff University researchers has uncovered a potential new way to treat a very rare genetic disorder that causes muscles in the arms and legs to become increasingly weak. GNE myopathy is a debilitating condition that affects young adults in their 20s or 30s, typically leaving them in a wheelchair within years. It… Read More »

Promising new sickle cell disease medicine wins FDA approval

This undated image provided by Novartis shows bottles of Novartis’s Adakveo. U.S. regulators have approved the new sickle cell disease medicine that can prevent extremely painful, dangerous “crises” in which misshapen blood cells clump together, reducing blood and oxygen flow. (Novartis via AP) After a recent decision by the FDA a better day could be… Read More »

‘No Longer a Disease for Our Moms and Grandmas’: Women on Early Breast Cancer

At the age of 41, Jenny Rose Ryan was shocked to learn she had breast cancer. In a recent Styles column, Jenny, a writer, editor and communications consultant in the Pacific Northwest, shared the story of her diagnosis with ductal carcinoma in situ, or D.C.I.S., and the emotions that followed. The piece inspired dozens of… Read More »